CRISPR gene editing already promises to fight diseases that were once considered invulnerable, but previously the tools had to be injected directly into the affected cells. This is not very practical for some conditions. However, there was just a breakthrough. NPR reports that researchers have released results showing that you can inject CRISPR-Cas9 into the … Read more
Scientists are trying to treat a growing number of rare diseases with gene therapy. It offers a potential one-off solution that attacks the root cause of the disease rather than just treating symptoms. (2th of June)
Sanath Kumar Ramesh with his son Raghav. (Courtesy photo of the Ramesh family) On a fine August day in a Bellevue park, Sanath Kumar Ramesh received a call from his son’s doctor as he was preparing to cut the cake for his little boy’s first birthday. He finally knew what was making his child sick, … Read more